orphanet

is a Data Source.

Orphanet is a unique resource for information and data on rare diseases and orphan drugs, aimed at improving diagnosis, care, and treatment of patients with rare diseases. It maintains the Orphanet rare disease nomenclature (ORPHAcodes), which is essential for improving the visibility of rare diseases in health and research information systems.

Domains

biomedical, clinical

License

CC BY 4.0

Homepage

orphanet

Repository

GitHub

Infores ID

infores:orphanet

FAIRsharing ID

Unknown

Product Summary

Products

From this Resource
ID Name URL Category Format Description
orphanet.portal Orphanet Portal www.orpha.net GraphicalInterface http Main Orphanet portal for rare disease...
orphanet.orphadata_science Orphadata Science Portal sciences.orphadata.com GraphicalInterface http Orphadata Science portal for Orphanet...
orphanet.scientific_knowledge_files Orphanet Scientific Knowledge Files orphanet-scientific-knowledge-files Product xml Orphanet scientific knowledge files f...
orphanet.ordo_release ORDO Release Page ordo DocumentationProduct http Current Orphadata Science page for th...
orphanet.expertcenters Expert Centers Dataset expert-resources Product xml XML dataset containing information on...
orphanet.expertcentersnetworks Expert Centers Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.diagnostictests Diagnostic Tests and Laboratories Dataset expert-resources Product xml XML dataset containing information on...
orphanet.patientorganizations Patient Organizations Dataset expert-resources Product xml XML dataset containing information on...
orphanet.patientorganizationsnetworks Patient Organizations Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.researchprojects National Research Projects Dataset expert-resources Product xml XML dataset containing information on...
orphanet.researchprojectsnetworks Multinational Research Projects Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.clinicaltrials National Clinical Trials Dataset expert-resources Product xml XML dataset containing information on...
orphanet.clinicaltrialsnetworks Multinational Clinical Trials Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.patientregistries Patient Registries Dataset expert-resources Product xml XML dataset containing information on...
orphanet.patientregistriesnetworks Patient Registries Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.biobanks Biobanks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.biobanksnetworks Biobanks Networks Dataset expert-resources Product xml XML dataset containing information on...
orphanet.orphandrugs Orphan Drugs Dataset expert-resources Product xml XML dataset containing information on...
orphanet.orphadataapi Orphadata API contact ProgrammingInterface http Contact point for API-mediated or req...
From other Resources
ID Name URL Category Format Relation Description
disgenet.data DisGeNET Data www.disgenet.com GraphProduct had primary source DisGeNET data, including gene to dise...
genecards.disease.associations GeneCards Disease Associations www.genecards.org Product http had primary source Disease association data integrated f...
medgen.ordo-history ORDO CUI History ORDO_CUI_history.txt (1.1 MB) Product txt had primary source History file tracking changes to Orph...
raras.portal Raras Portal raras.org GraphicalInterface http was informed by Main Raras portal for searching rare ...
raras.encyclopedia Raras Encyclopedia explorar GraphicalInterface http was informed by Rare disease encyclopedia for browsin...
oregano.graph OREGANO Knowledge Graph Graphs GraphProduct http was derived from The OREGANO knowledge graph dataset i...
eram.web eRAM Web Interface eram GraphicalInterface http was informed by Web-based interface for browsing and ...
eram.downloads eRAM Data Downloads download.php Product mixed was derived from Downloadable data files containing ra...
biobtree.api BioBTree REST API api ProgrammingInterface http had primary source REST API for searching identifiers an...

Details

Orphanet

Orphanet is a unique resource gathering and improving knowledge on rare diseases to enhance diagnosis, care, and treatment of patients with rare diseases. It aims to provide high-quality information on rare diseases and ensure equal access to knowledge for all stakeholders.

Overview

Established in France by INSERM (French National Institute for Health and Medical Research) in 1997, Orphanet has evolved into a European endeavor, gradually growing to a Consortium of 40 countries worldwide. The Orphanet database contains information on:

  • 6,528+ rare diseases
  • 4,512+ genes
  • 8,722+ expert centers
  • 36,595+ diagnostic tests
  • 30,456+ professionals These counts are historical context from earlier Orphanet summaries and may differ from the current public portal.

Key Resources

Orphanet Rare Disease Ontology (ORDO)

ORDO is a structured vocabulary for rare diseases derived from the Orphanet database. It captures relationships between diseases, genes, and other relevant features, providing integrated, re-usable data for computational analysis. The ontology is maintained by Orphanet and follows OBO guidelines.

ORPHAcodes - Orphanet Nomenclature

The Orphanet nomenclature is a multilingual, standardized, controlled medical terminology specific to rare diseases. Each clinical entity is associated with a unique numerical identifier (ORPHAcode), preferred term, synonyms, and definition. The nomenclature pack includes files for implementing ORPHAcodes in health information systems.

Orphanet Scientific Knowledge Base

This comprehensive collection of datasets provides structured information about rare diseases, including:

  • Disease alignments with other terminologies (ICD-10, ICD-11, OMIM, UMLS, MONDO, MeSH, MedDRA, GARD)
  • Classifications of rare diseases
  • Gene associations
  • Clinical signs and symptoms
  • Functional consequences
  • Epidemiological data
  • Natural history information

Recognition

Orphadata Science (which includes ORDO and the scientific knowledge files) has been recognized as:

  • An ELIXIR Core Data Resource
  • A Global Core Biodata Resource
  • An IRDiRC Recognized Resource

Data Access

All Orphanet data resources are available under the Creative Commons Attribution 4.0 International (CC BY 4.0) license, making them freely accessible for research and implementation. Data are updated bi-annually in July and December; the current Orphadata Science pages checked during this curation listed December 2025 releases for the scientific knowledge files and ORDO 4.8.

Is this information incorrect or incomplete? Request an update.

Created: July 10, 2025 | Last modified: June 02, 2026